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Denise A. Carbonaro, Ph.D. - Publications

Affiliations: 
2009 Biology University of Southern California, Los Angeles, CA, United States 
Area:
Microbiology Biology, Cell Biology, Genetics
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21 high-probability publications. We are testing a new system for linking publications to authors. You can help! If you notice any inaccuracies, please sign in and mark papers as correct or incorrect matches. If you identify any major omissions or other inaccuracies in the publication list, please let us know.

Year Citation  Score
2017 Shaw KL, Garabedian E, Mishra S, Barman P, Davila A, Carbonaro D, Shupien S, Silvin C, Geiger S, Nowicki B, Smogorzewska EM, Brown B, Wang X, de Oliveira S, Choi Y, et al. Clinical efficacy of gene-modified stem cells in adenosine deaminase-deficient immunodeficiency. The Journal of Clinical Investigation. PMID 28346229 DOI: 10.1172/Jci90367  0.451
2016 Punwani D, Kawahara M, Yu J, Sanford U, Roy S, Patel K, Carbonaro DA, Karlen AD, Khan S, Cornetta KG, Rothe M, Schambach A, Kohn DB, Malech HL, McIvor RS, et al. Lentivirus Mediated Correction of Artemis-deficient Severe Combined Immunodeficiency. Human Gene Therapy. PMID 27611239 DOI: 10.1089/Hum.2016.064  0.44
2014 Carbonaro DA, Zhang L, Jin X, Montiel-Equihua C, Geiger S, Carmo M, Cooper A, Fairbanks L, Kaufman ML, Sebire NJ, Hollis RP, Blundell MP, Senadheera S, Fu PY, Sahaghian A, et al. Preclinical demonstration of lentiviral vector-mediated correction of immunological and metabolic abnormalities in models of adenosine deaminase deficiency. Molecular Therapy : the Journal of the American Society of Gene Therapy. 22: 607-22. PMID 24256635 DOI: 10.1038/Mt.2013.265  0.527
2012 Candotti F, Shaw KL, Muul L, Carbonaro D, Sokolic R, Choi C, Schurman SH, Garabedian E, Kesserwan C, Jagadeesh GJ, Fu PY, Gschweng E, Cooper A, Tisdale JF, Weinberg KI, et al. Gene therapy for adenosine deaminase-deficient severe combined immune deficiency: clinical comparison of retroviral vectors and treatment plans. Blood. 120: 3635-46. PMID 22968453 DOI: 10.1182/Blood-2012-02-400937  0.486
2012 Carbonaro DA, Jin X, Wang X, Yu XJ, Rozengurt N, Kaufman ML, Wang X, Gjertson D, Zhou Y, Blackburn MR, Kohn DB. Gene therapy/bone marrow transplantation in ADA-deficient mice: roles of enzyme-replacement therapy and cytoreduction. Blood. 120: 3677-87. PMID 22833548 DOI: 10.1182/Blood-2012-02-408591  0.482
2008 Carbonaro DA, Jin X, Cotoi D, Mi T, Yu XJ, Skelton DC, Dorey F, Kellems RE, Blackburn MR, Kohn DB. Neonatal bone marrow transplantation of ADA-deficient SCID mice results in immunologic reconstitution despite low levels of engraftment and an absence of selective donor T lymphoid expansion. Blood. 111: 5745-54. PMID 18356486 DOI: 10.1182/Blood-2007-08-103663  0.431
2007 Engel BC, Podsakoff GM, Ireland JL, Smogorzewska EM, Carbonaro DA, Wilson K, Shah A, Kapoor N, Sweeney M, Borchert M, Crooks GM, Weinberg KI, Parkman R, Rosenblatt HM, Wu SQ, et al. Prolonged pancytopenia in a gene therapy patient with ADA-deficient SCID and trisomy 8 mosaicism: a case report. Blood. 109: 503-6. PMID 16973956 DOI: 10.1182/Blood-2006-06-031476  0.507
2006 Carbonaro DA, Jin X, Petersen D, Wang X, Dorey F, Kil KS, Aldrich M, Blackburn MR, Kellems RE, Kohn DB. In vivo transduction by intravenous injection of a lentiviral vector expressing human ADA into neonatal ADA gene knockout mice: a novel form of enzyme replacement therapy for ADA deficiency. Molecular Therapy : the Journal of the American Society of Gene Therapy. 13: 1110-20. PMID 16651028 DOI: 10.1016/J.Ymthe.2006.02.013  0.465
2005 Podsakoff GM, Engel BC, Carbonaro DA, Choi C, Smogorzewska EM, Bauer G, Selander D, Csik S, Wilson K, Betts MR, Koup RA, Nabel GJ, Bishop K, King S, Schmidt M, et al. Selective survival of peripheral blood lymphocytes in children with HIV-1 following delivery of an anti-HIV gene to bone marrow CD34(+) cells. Molecular Therapy : the Journal of the American Society of Gene Therapy. 12: 77-86. PMID 15963923 DOI: 10.1016/J.Ymthe.2005.02.024  0.482
2005 Kobayashi H, Carbonaro D, Pepper K, Petersen D, Ge S, Jackson H, Shimada H, Moats R, Kohn DB. Neonatal gene therapy of MPS I mice by intravenous injection of a lentiviral vector. Molecular Therapy : the Journal of the American Society of Gene Therapy. 11: 776-89. PMID 15851016 DOI: 10.1016/J.Ymthe.2004.10.006  0.459
2005 Blumenthal M, Skelton D, Carbonaro DA, Pepper KA, Kohn DB. 805. Effective Suicide Gene Therapy of Leukemia in a Novel Model of Retroviral Insertion Molecular Therapy. 11. DOI: 10.1016/J.Ymthe.2005.07.342  0.475
2005 Carbonaro DA, Jin X, Petersen D, Kohn DB. 37. A Novel Form of Enzyme Replacement Therapy for ADA-Deficiency: In Vivo Transduction by Neonatal Injection of Lentivirus Expressing ADA Molecular Therapy. 11. DOI: 10.1016/J.Ymthe.2005.06.037  0.518
2004 Jin X, Carbonaro DA, Senadherra D, Petersen D, Kwan S, Kohn DB. 905. The endogenous WASp promoter fragments in SIN lentiviral vectors drive expression preferentially in T cells Molecular Therapy. 9. DOI: 10.1016/J.Ymthe.2004.06.811  0.389
2004 Kobayashi H, Petersen D, Carbonaro D, Skelton D, Ge S, Luzko C, Cannon P, Dussel MO, Rosol M, Moats R, Shimada H, Kohn DB. 696. Comparative study of lentiviral vector-mediated gene therapy in neonatal and young-adult MPS I mice by a single intravenous injection Molecular Therapy. 9. DOI: 10.1016/J.Ymthe.2004.06.647  0.447
2004 Carbonaro DA, Jin X, Senadherra D, Pepper K, Petersen D, Yu X, Skelton D, Kohn DB. 177. Lentiviral Vector Mediated ADA Gene Transfer in ADA-Deficient SCID Mice Molecular Therapy. 9. DOI: 10.1016/J.Ymthe.2004.06.137  0.559
2003 Schmidt M, Glimm H, Wissler M, Hoffmann G, Olsson K, Sellers S, Carbonaro D, Tisdale JF, Leurs C, Hanenberg H, Dunbar CE, Kiem HP, Karlsson S, Kohn DB, Williams D, et al. Efficient characterization of retro-, lenti-, and foamyvector-transduced cell populations by high-accuracy insertion site sequencing. Annals of the New York Academy of Sciences. 996: 112-21. PMID 12799289 DOI: 10.1111/J.1749-6632.2003.Tb03239.X  0.4
2003 Schmidt M, Carbonaro DA, Speckmann C, Wissler M, Bohnsack J, Elder M, Aronow BJ, Nolta JA, Kohn DB, von Kalle C. Clonality analysis after retroviral-mediated gene transfer to CD34+ cells from the cord blood of ADA-deficient SCID neonates. Nature Medicine. 9: 463-8. PMID 12640448 DOI: 10.1038/Nm844  0.504
2002 Price MA, Case SS, Carbonaro DA, Yu XJ, Petersen D, Sabo KM, Curran MA, Engel BC, Margarian H, Abkowitz JL, Nolan GP, Kohn DB, Crooks GM. Expression from second-generation feline immunodeficiency virus vectors is impaired in human hematopoietic cells. Molecular Therapy : the Journal of the American Society of Gene Therapy. 6: 645-52. PMID 12409263 DOI: 10.1016/S1525-0016(02)90725-2  0.489
2000 Bauer G, Selander D, Engel B, Carbonaro D, Csik S, Rawlings S, Church J, Kohn DB. Gene therapy for pediatric AIDS Annals of the New York Academy of Sciences. 918: 318-329. PMID 11131719 DOI: 10.1111/J.1749-6632.2000.Tb05501.X  0.529
1999 Kohn DB, Bauer G, Rice CR, Rothschild JC, Carbonaro DA, Valdez P, Hao Ql, Zhou C, Bahner I, Kearns K, Brody K, Fox S, Haden E, Wilson K, Salata C, et al. A clinical trial of retroviral-mediated transfer of a rev-responsive element decoy gene into CD34(+) cells from the bone marrow of human immunodeficiency virus-1-infected children. Blood. 94: 368-71. PMID 10381536 DOI: 10.1182/Blood.V94.1.368.413A47_368_371  0.538
1998 Wang L, Robbins PB, Carbonaro DA, Kohn DB. High-resolution analysis of cytosine methylation in the 5' long terminal repeat of retroviral vectors Human Gene Therapy. 9: 2321-2330. PMID 9829531 DOI: 10.1089/Hum.1998.9.16-2321  0.414
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