Christian L. Lorson

University of Missouri - Columbia, Columbia, MO, United States 
Microbiology Biology, Neuroscience Biology, Molecular Biology, Genetics
"Christian Lorson"
BETA: Related publications


You can help our author matching system! If you notice any publications incorrectly attributed to this author, please sign in and mark matches as correct or incorrect.

Shababi M, Smith CE, Kacher M, et al. (2019) Development of a novel severe mouse model of spinal muscular atrophy with respiratory distress type 1: FVB-nmd. Biochemical and Biophysical Research Communications
Kaifer KA, Villalón E, O'Brien BS, et al. (2019) AAV9-Mediated Delivery of miR-23a Reduces Disease Severity in Smn2B-/SMA Model Mice. Human Molecular Genetics
Shababi M, Villalón E, Kaifer KA, et al. (2018) A Direct Comparison of IV and ICV Delivery Methods for Gene Replacement Therapy in a Mouse Model of SMARD1. Molecular Therapy. Methods & Clinical Development. 10: 348-360
Villalón E, Shababi M, Kline R, et al. (2017) Selective vulnerability in neuronal populations in nmd/SMARD1 mice. Human Molecular Genetics
Rindt H, Tom CM, Lorson CL, et al. (2017) Optimization of trans-Splicing for Huntington's Disease RNA Therapy. Frontiers in Neuroscience. 11: 544
Shababi M, Feng Z, Villalon E, et al. (2016) Rescue of a Mouse Model of Spinal Muscular Atrophy with Respiratory Distress type 1 (SMARD1) by AAV9-IGHMBP2 is Dose Dependent. Molecular Therapy : the Journal of the American Society of Gene Therapy
Rindt H, Feng Z, Mazzasette C, et al. (2015) Astrocytes influence the severity of spinal muscular atrophy. Human Molecular Genetics. 24: 4094-102
Seng CO, Magee C, Young PJ, et al. (2015) The SMN structure reveals its crucial role in snRNP assembly. Human Molecular Genetics. 24: 2138-46
Osman EY, Miller MR, Robbins KL, et al. (2014) Morpholino antisense oligonucleotides targeting intronic repressor Element1 improve phenotype in SMA mouse models. Human Molecular Genetics. 23: 4832-45
Robbins KL, Glascock JJ, Osman EY, et al. (2014) Defining the therapeutic window in a severe animal model of spinal muscular atrophy. Human Molecular Genetics. 23: 4559-68
See more...